Marathon Pharmaceuticals Pauses Commercialization of EMFLAZA to Address Concerns of Duchenne Community

Today, Marathon Pharmaceuticals, maker of the recently FDA-approved drug EMFLAZA, announced that they are pausing commercialization efforts in order to address the concerns about price and access to the drug from the Duchenne muscular dystrophy community. MDA will update our community with more information as it becomes available. We remain committed to ensuring that our families have the resources and assistance to begin and maintain treatments with emerging therapies for neuromuscular diseases.

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Raymond Walter: Brilliant U of A Graduate Student with DMD Lives Unlimited By Pursuing His Passions

Raymond (Ray) Walter, who has Duchenne muscular dystrophy, graduated college with degrees in physics, mathematics and economics at age 18. He is currently continuing his doctoral studies in mathematics and physics at the University of Arkansas, where he is a Distinguished Doctoral Fellow and National Science Foundation Graduate Research Fellow. Raymond has also recently been . . .

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Scarlett’s Night at MDA Muscle Team Gala

Hockey season is finally underway, and the Chicago Blackhawks have added one more fan to their roster. No, this fan is not a burly teenager who loves to play hockey, or someone mesmerized by the Blackhawks and their Stanley Cup glory of the past six years. This fan is 5-year-old Scarlett Sepe, an adorably outgoing . . .

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