Tag: Advances in Treatment

Adults, Research, Living with Muscular Dystrophy

FDA Approves Alexion’s Ultomiris for Treatment of gMG

Sujatha Gurunathan

On April 28, the US Food and Drug Administration (FDA) granted approval to ravulizumab (Ultomiris) for the treatment of generalized myasthenia gravis (gMG) in adults who test positive for the anti-acetylcholine receptor (AChR) antibody. To date, Ultomiris is the third disease modifying drug approved to treat gMG. Ultomiris will be made available in the United . . .

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Kids, Young Adults, News, Research, Living with Muscular Dystrophy

Researchers Announce Results from a Phase 3 Study of Corticosteroid Dosing to Treat DMD

Sujatha Gurunathan

On April 5, an international research team, headed by Michela Guglieri at Newcastle University and Robert Griggs at the University of Rochester Medical Center, announced positive results at the American Academy of Neurology (AAN meeting) in Seattle, WA from the phase 3 FOR DMD study of corticosteroid dosing regimens for treatment of people with Duchenne . . .

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