On Sept. 24, we held our annual Becker Muscular Dystrophy (BMD) Conference aimed at connecting families with researchers and other individuals living with BMD. The conference took place in Washington, D.C., and featured a wide range of topics that included understanding the root causes of BMD, how genetics and other factors contribute to the variation . . .
Last week, MDA’s Emergency Preparedness Webinar explored how important it is for individuals with disabilities or with access and functional needs to design a personalized emergency plan for themselves and their families so they are prepared and empowered to handle any kind of emergency or disaster. If you were unable to join last week’s webinar, . . .
Allison Willis and her sons, Nolan and Jack (15), who participated in the clinical trials for the exon-skipping drug Exondys 51 (eteplirsen), react to the FDA’s approval and expanded use of the drug. The drug treats Duchenne muscular dystrophy. Watch the video of their story and the groundbreaking clinical trial that made history:
A couple of years ago MDA got to know the Somers family… While Crystal and Cooper continue to mourn the loss of an incredible husband and father, they are able to focus on and appreciate the positives in their life now. Cooper recently turned 6, started first grade and is ready – and excited – . . .
