An expression of the live unlimited spirit, stories and voices of the MDA community
Since 1986, when MDA-funded researchers identified the gene that, when flawed, leads to Duchenne muscular dystrophy (DMD), scientists have been actively pursuing treatments and cures. In the past 12 months, MDA has awarded research grants to the following individuals who are building on the strong foundation of previous research and discovery to better understand — and someday cure — the diseases.
There’s so much in store for the year ahead, and we’re so grateful you’re with us.
As we celebrate the new year, former MDA National Ambassador Joe Akmakjian takes the time to celebrate accomplishments of the past while looking forward to the opportunities that lie ahead.
Researchers are looking for individuals with SMA type 2 to participate in the phase 1 STRONG clinical trial, to test safety, dosing and proof of concept for efficacy for its SMA gene replacement therapy AVXS-101.
Andrew Lieberman of the University of Michigan Medical School was awarded an MDA research grant to test a modified antisense oligonucleotide (ASO) therapy to treat spinal-bulbar muscular atrophy.
Olivia and Steven Sosa are grateful for MDA Muscle Walk, which allows them to raise awareness & funds for MDA families.
In 2017, MDA helped thousands of families live better and longer lives. All of this and much more was possible thanks to you. Thank you for helping MDA make 2017 a remarkable year for the families we serve.
NALC member Julie Turney is determined to help MDA families live longer and grow stronger.
Auinash Kalsotra of the University of Illinois was awarded an MDA research grant totaling $300,000 over three years to shed light on how defects develop in the heart in DM1.
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