Genetic Testing: Knowledge is Power
Andrew Boychuk, who lives with LGMD, shares the positive impact MDA’s LGMD genetic testing program has made in his life.
Category: Research
Impassioned by Science, Motivated by Love: Behind the Scenes at the 4th Annual Strength, Science and Stories of Inspiration
Chris Anselmo, who lives with an NMD, reports back from the 4th annual Strength, Science and Stories of Inspiration (SSSI)
FDA Grants Orphan Drug Designation to Stealth BioTherapeutics’ Experimental Mitochondrial Myopathy Drug Elamipretide
Elamipretide, which treats muscle weakness caused by mitochondrial disease, has received FDA Orphan Drug Designation
Five Questions with Researcher Maya Maor Nof
Maya Maor Nof of Stanford University School of Medicine received the 2017 SSSI-MDA Fellowship Award to study ALS.
LGMD Genetic Testing Program: What You Need to Know
Do you or a loved one live with LGMD? Learn more about MDA’s LGMD genetic testing program and find out how to make an impact on LGMD research.
Five Questions with Researcher Marshall Hogarth
Dr. Marshall Hogarth was awarded an MDA grant to research LGMD2B and Miyoshi myopathy.
Five Questions with FA Researcher Manuela Corti
Manuela Corti of University of Florida was awarded an MDA grant to study gene therapy in FA
Five Questions with Researcher Eduardo Balsa Martinez
Learn about Dr. Eduardo Balsa Martinez’s research to idenitfy therapeutic targets in mitochondrial diseases.
Five Questions with Researchers Nigel Laing, Kristen Nowak and Rhonda Taylor
Dr. Nigel Laing was awarded an MDA research grant to test two potential treatments for McArdle disease.
CENTAUR ALS Trial Seeks Participants
Researchers are looking for people with ALS to join a clinical trial to test the drug AMX0035.
