Over 500 of the sharpest minds in research have gathered at MDA’s Scientific Conference as they work to unlock the secrets of neuromuscular diseases.
Researchers are looking for people to participate in a clinical trial, sponsored by Cedars-Sinai Medical Center, to test the safety and efficacy of beetroot juice extract in people with BMD.
Researchers are looking for people to participate in a phase 2 clinical trial, sponsored by Neuraltus Pharmaceuticals, that is designed to test whether the investigational drug NP001 slows progression of signs and symptoms in ALS.
This week, hundreds of the best and brightest scientists from around the country are gathering in the Washington, D.C., area at the 2017 MDA Scientific Conference, with the goal of working collectively toward advancing scientific breakthroughs to save and improve lives for MDA families.
New research, supported by MDA and the CMT Association, examines gene therapy in CMT.
Alexion Pharma announced the FDA will review its investigational drug eculizumab (brand name Soliris) for treatment of refractory generalized MG.
MDA has awarded an MDA Venture Philanthropy (MVP) grant to Izumi Biosciences, Inc., to fund early-stage development of IZ10023, for use in people with ALS who are taking riluzole, the only drug approved by the U.S. Food and Drug Administration to treat ALS.
For this latest round of awards, MDA reviewed 187 applications and had sufficient funds to approve funding for approximately 15 percent of them — 29 grants with a total funding commitment of more than $7 million.
Following the approval of three drugs in six months, new MDA grants push for more progress By Grace Pavlath, Ph.D., MDA Senior Vice President & Scientific Program Director What are the effects of steroids on muscle repair in patients with Duchenne muscular dystrophy (DMD)? How can gene therapy impact people with Charcot-Marie-Tooth disease (CMT)? Will . . .
The FDA has approved Marathon Pharmaceuticals’ new drug applications for deflazacort (brand name Emflaza) to treat Duchenne Muscular Dystrophy
