An expression of the live unlimited spirit, stories and voices of the MDA community
In recognition of National Disability Employment Awareness Month, Chris and Sean, who both work for Microsoft and live with MD, share what has helped them succeed in their careers.
Congress has voted to extend the FAA’s tax authority for six months. As anticipated, the extension did not include any of the disability provisions set out in the full bill, but the possibility of these provisions being included in the full reauthorization in March remains.
Meet fire fighter DuWayne Schwartz, who says “more is more” when it comes to supporting MDA families.
PTC Therapeutics President and CEO Stuart Peltz, Ph.D., issued a letter to the DMD community after the FDA declined to approve ataluren (brand name Translarna) for the treatment of DMD.
PTC Therapeutics reported today the U.S. Food and Drug Administration’s Office of Drug Evaluation is unable to approve the company’s New Drug Application for ataluren (brand name Translarna) for the treatment of Duchenne muscular dystrophy (DMD) caused by a premature stop codon, or nonsense mutation, in its current form.
Andrew Boychuk, who lives with LGMD, shares the positive impact MDA’s LGMD genetic testing program has made in his life.
FDA: Soliris is approved to treat adults with generalized MG.
Chris Anselmo, who lives with an NMD, reports back from the 4th annual Strength, Science and Stories of Inspiration (SSSI)
The Wood family, whose son George lives w LGMD, has raised thousands of dollars for MDA by cooking jambalaya.
The drug therapy ATB200/AT2221, meant to treat Pompe disease, has received FDA Orphan Drug Designation.
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