At the 2019 MDA Clinical & Scientific Conference, one scientific session of interest centered on what’s new in neuromuscular diseases (NMDs). In this session, presenting scientists discussed progress in therapy development and clinical trials for a range of NMDs, including Becker muscular dystrophy (BMD), congenital muscular dystrophy (CMD), congenital myasthenic syndromes (CMS), myotonic dystrophy (DM), . . .
Early identification and treatment for neuromuscular disorders are essential to optimize health outcomes. Newborn screening, which identifies health issues via a blood test taken soon after birth, is essential to ensure that infants born with serious but treatable disorders have the best possible chance at receiving the care and support services they need as early . . .
Patrick Cusick’s journey with MDA — and with muscular dystrophy — started 12 years ago, in, of all places, a life insurance office. Twenty-nine at the time, the Ohio native and his wife were expecting their first child, and making preparations as parents (or soon-to-be parents) do. Securing life insurance meant taking some medical tests; . . .
Researchers at the State University of New York at Binghamton’s School of Pharmacy and Pharmaceutical Sciences are seeking participants living with Becker muscular dystrophy (BMD) to participate in a biomarker and patient-reported outcomes study. The purpose of the Becker Muscular Dystrophy Biomarker and Patient-Reported Outcomes Study is to learn more about disease progression in patients . . .
Bryan Steward, who lives with Becker muscular dystrophy, set out to hike the 500-mile Camino de Santiago in Northern Spain last month. As he nears the end of his journey, he checked in again with us to update us on his progress. Justin Skeesuck and Patrick Gray, two other Camino hikers whose film I’ll Push You will be released in a one-night only screening at select theaters nationwide on November 2 and will benefit MDA, respond to Bryan’s entries with wisdom from their own journey.
Bryan Steward, who lives with Becker muscular dystrophy, is hiking the 500-mile Camino de Santiago in Northern Spain, and he just checked in with us to update us on his progress. Justin Skeesuck and Patrick Gray, two other Camino hikers whose film I’ll Push You will be released in a one-night only screening at select theaters nationwide on November 2 and will benefit MDA, respond to Bryan with memories from their own journey.