Trial to Test Drug Targeting Muscle Cramps Seeks Participants
Researchers are looking for people with MNDs like ALS to join a clinical trial for the investigational drug FLX-787-ODT.
Tag: Clinical Trials
Participants Sought for FORTITUDE ALS Trial
Researchers are looking for people with ALS to participate in a phase 2 clinical trial for the investigational drug CK-2127107.
Participants Sought for FIREFISH SMA Study
Researchers are looking for individuals with type 1 SMA for a clinical trial to test the investigational drug RG7916.
Participants Sought for SMA Gene Therapy Study
Researchers are looking for individuals with type 1 SMA to test efficacy for its SMA gene replacement therapy AVXS-101.
CENTAUR ALS Trial Seeks Participants
Researchers are looking for people with ALS to join a clinical trial to test the drug AMX0035.
Participants Sought for ACE-083 CMT Study
Researchers are looking for people with CMT to participate in a phase 2 clinical trial, sponsored by Acceleron Pharma.
Participants Sought for Answer ALS Study
Researchers are looking for people to participate in the Answer ALS: Individualized Initiative for ALS Discovery study.
Spinraza Helps Young Woman Participate in Muscle Walk — and She Thinks You Should, Too
Kate, who lives with SMA type 3 and has directly benefited from, Spinraza, a medication that can trace its root back to MDA, encourages supporters to go the distance for MDA via their local MDA Muscle Walks.
Promising results in phase 1 SMA gene therapy trial
Chicago-based biotechnology company AveXis has announced encouraging results from its completed phase 1 gene therapy trial to test the investigational therapy AVXS-101 in infants with type 1 SMA.
Encouraging Trial Data Reported for ALS Drug Masitinib
AB Science has reported encouraging top line trial results from its completed phase 2/3 study in Europe of the experimental drug masitinib in ALS. Additional testing is likely required, but if successful, masitinib could one day become an approved therapy for ALS.
