Researchers at the University of California, Davis Neuromuscular Research Lab are seeking individuals with or without neuromuscular disease (ages 2 years or older) to participate in a research study to test the feasibility of using a wearable gait sensor to collect data as part of a new outcome measure for use in future clinical trials. This . . .
The Muscular Dystrophy Association recently awarded an MDA clinical research network grant to develop and maintain a core facioscapulohumeral muscular dystrophy (FSHD) Clinical Trial Research Network (CTRN). The investment, totaling $1.2 million over three years, supports seven medical centers that specialize in FSHD research and clinical care and is targeted to spur advances in FSHD . . .
Growing up, Marc van de Rijn was always interested in medicine. After briefly considering a career working with computers, a sudden health challenge after his freshman year of college made him realize that instead of sitting behind a desk, he wanted to work with people and become a doctor. “After my freshman year, I suffered . . .
During 2017 we were honored to provide four research grants and one development grant to individuals looking to accelerate treatments and cures for FSHD and FA. Learn more about their work:
Acceleron Pharma announced encouraging preliminary results from its phase 2 clinical trial to test the experimental drug ACE-083 in FSHD.
Angela Lek, a postdoctoral research fellow at Boston Children sHospital, was awarded an MDA development grant totaling $180,000 over three years to use cutting-edge techniques and a novel approach to search for drug targets in FSHD.
Meet Lauren McLane, a young adult living with FSHD who’s exploring her independence with some help from SYNERGY HomeCare.
Dr. Charles Emerson was awarded an MDA research grant to study FSHD.
Learn how the Yoken family fights back against FSHD, one hop at a time.
MDA awarded a research grant to Scott Harper of Ohio State University to test a gene therapy for FSHD.
