Today, more than 60 buildings and landmarks across the U.S. and Canada will be lit bright green to raise awareness for neuromuscular diseases thanks to Light It Up Green for Muscular Dystrophy.
Joe Akmakjian shares highlights from his interview with MDA grant recipient Mattia Quattrocelli.
Parents of young boys with DMD, as well as parents of age-matched non-affected boys, are being sought to participate in an online observational study.
DMD Families are invited to an Emflaza webinar in partnership with PTC Therapeutics on July 6.
This Father’s Day, we’re recognizing an extraordinary MDA dad. Josh Argall was initially devastated by his son Devin’s DMD diagnosis, but once the shock wore off, he resolved to do everything he could for his son and all MDA families. “I can’t discover the new medicine, I can’t provide healthcare, but I can contribute to the mission in my own way, so that’s what I decided to do…There isn’t anything I wouldn’t do for MDA. Knowing how these parents feel and these children feel, that’s what keeps me going.”
Trayton, who lives with DMD, is the first boy in Montana to receive the breakthrough DMD treatment Exondys 51
Take a look at some of the most heartwarming MDA Team Momentum stories guaranteed to give you all of the feels.
Translarna, a new drug under development that may slow functional decline in individuals with DMD cause by nonsense mutations, will be reviewed by an Advisory Committee of the U.S. Food and Drug Administration on Sept. 28, 2017. An FDA decision on the drug is expected on or before Oct. 24, 2017.
The Moctezumas share how they have become experts at caring for their 25-year old son, Michael, who lives with DMD.
Find answers to your questions about access, cost and availability of DMD drug Emflaza.
